Restoring hope for people affected by CNS disorders
Our mission is to improve life health for people affected by CNS disorders by driving the regenerative power of the human body
We aim to restore hope for people affected by both rare and prevalent diseases by creating the next generation of regenerative medicines for the brain. By restoring the brain to a healthier state these therapies will address the progressive and debilitating course of these conditions, allowing people to live the futures they deserve.
Creating Next Generation Therapies for CNS Disorders
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Our brain-targeting chemistry platform creates orally administered small molecule prodrugs with tunable ratios of central vs. peripheral exposure. This approach enables us to develop molecules with bespoke distribution profiles tailored to match disease pathophysiology.
Our portfolio is anchored by high-confidence programs that leverage established clinical precedence, human genetics and biology, de-risking our pipeline and accelerating early development.
Our programs utilize biomarker-driven development strategies to demonstrate on-target / on-tissue activity and proof-of-mechanism early in the clinic.